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Please make checks payable to Zoja Research Foundation.

Mail to:
Zoja Research Foundation
3937 Spring Garden Dr
Colleyville, TX 76034

Write “SMG9 research” on the memo line. Email enicaj1@gmail.com after you send it so we can confirm and send a receipt.

Fund SMG9 Research: Model, Candidates, and Lead SelectionZoja Research Foundation is funding a gene-replacement program for SMG9 deficiency, an ultra-rare genetic disorder. There is currently no treatment.This campaign raises $455,000 for the current study at the University of Missouri with Dr. J. Andrea Sierra-Delgado. That work will:<ul fr-original-style="" style="box-sizing: inherit;"><li fr-original-style="" style="box-sizing: inherit;">Build a patient-specific mouse model and patient-derived cell lines</li><li fr-original-style="" style="box-sizing: inherit;">Develop and compare two research-grade gene therapy candidates</li><li fr-original-style="" style="box-sizing: inherit;">Select a lead construct</li><li fr-original-style="" style="box-sizing: inherit;">Run a preliminary safety study in mice</li><li fr-original-style="" style="box-sizing: inherit;">Prepare for a pre-IND conversation with the FDA</li></ul>Our family is personally funding the start of this phase. Donations help complete it.If this phase succeeds, a later campaign will cover clinical-grade manufacturing and remaining IND-enabling studies, estimated at $1&ndash;$1.5 million.Zoja Research Foundation is a 501(c)(3) nonprofit. Donations are tax-deductible to the extent allowed by law.

Hello <span contenteditable="false" data-custom-variable="{{firstname}}" fr-original-class="fr-deletable styled-tag-chip" fr-original-style="" style="color: rgb(42, 42, 196); overflow-wrap: anywhere; user-select: none; background-color: rgb(248, 248, 255); border: 1px solid rgb(191, 191, 255); border-radius: 4px; margin: 0px; padding: 1px 8px; font-size: 11px; display: inline-block; box-sizing: inherit;">First name, Thank you for your gift to Zoja Research Foundation. It goes directly to the SMG9 research program at the University of Missouri, including the models, gene-therapy candidates, and lead-selection work now underway. Zoja Research Foundation is a 501(c)(3) nonprofit. No goods or services were provided in exchange for this donation. Please keep this email for your records.We are grateful you&rsquo;re standing with us. Kristafer &amp; Elizabeth Nicaj

Fund SMG9 Research: Model, Candidates, and Lead SelectionZoja Research Foundation is funding a gene-replacement program for SMG9 deficiency, an ultra-rare genetic disorder. There is currently no treatment.This campaign raises $455,000 for the current study at the University of Missouri with Dr. J. Andrea Sierra-Delgado. That work will:<ul><li>Build a patient-specific mouse model and patient-derived cell lines</li><li>Develop and compare two research-grade gene therapy candidates</li><li>Select a lead construct</li><li>Run a preliminary safety study in mice</li><li>Prepare for a pre-IND conversation with the FDA</li></ul>Our family is personally funding the start of this phase. Donations help complete it.If this phase succeeds, a later campaign will cover clinical-grade manufacturing and remaining IND-enabling studies, estimated at $1–$1.5 million.Zoja Research Foundation is a 501(c)(3) nonprofit. Donations are tax-deductible to the extent allowed by law.

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